Our Pipeline

Our rapidly advancing clinical programs in Duchenne muscular dystrophy, Marburg and influenza represent the foundation for a growing and diverse pipeline in rare and infectious diseases.

 
 
 
 

Our therapeutic development programs include lead clinical candidates for Duchenne muscular dystrophy, hemorrhagic fever viruses and influenza.

  • PROGRAM
  • DISCOVERY
  • preclinical
  • PHASE 1
  • PHASE 2
  • PHASE 3
 

RARE DISEASES

  • ETEPLIRSEN (AVI-4658)
    DMD (EXON 51)
  • SRP-4053
    DMD (EXON 53)
  • SRP-4045
    DMD (EXON 45)
  • SRP-4050
    DMD (EXON 50)
  • SRP-4044
    DMD (EXON 44)
  • SRP-4052
    DMD (EXON 52)
  • SRP-4055
    DMD (EXON 55)
  • SRP-4008
    DMD (EXON 8)
  • UNDISCLOSED TARGETS
    NON-DMD
 
 

INFECTIOUS DISEASES

  • AVI-7288
    MARBURG VIRUS
  • AVI-7537
    EBOLA VIRUS
  • AVI-7100
    INFLUENZA
  • VIRAL PMO-X
    DENGUE
  • BACTERIAL PPMO
    TB
  • UNDISCLOSED TARGETS