Sarepta’s industry leading pipeline is comprised of over 40 programs in various stages of development across 3 technologies, RNA, gene therapy and gene editing, and multiple therapeutic areas including neuromuscular, CNS and cardiology. Currently, Sarepta has one gene therapy and three RNA-based therapies on the market in the United States.
¹Peptide phosphorodiamidate morpholino oligomers
²Other exon targets in development: 44, 45, 50, 52, and 53
³Other LGMD targets in development: SRP-9005 (LGMD2C/R5 γ-sarcoglycan), SRP-9006 (LGMD2L/R12 Anoctamin 5), and SRP-9010 (LGMD2A/R1)