• Program
  • Discovery
  • Preclinical
  • Phase I
  • Phase II
  • Phase III
  • Commercial*
EXONDYS 51 (eteplirsen)*
Golodirsen (SRP-4053)
Casimersen (SRP-4045)
Exon 52
Other Exon Targets**
SRP-5051
SRP-5053
SRP-5045
SRP-5052
SRP-5044
SRP-5050
Ezutromid (Summit)
GALGT2 (Nationwide)
Micro-Dystrophin (Nationwide)
Micro-Dystrophin (Genethon)
CRISPR/CAS9 (DUKE UNIVERSITY)